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January 21, 2016January 25, 2016

Cystic Fibrosis Treatment Granted FDA Orphan Drug Status

Cystic Fibrosis, News

Boulder, Colorado-based Nivalis Therapeutics recently announced the U.S. Food and Drug Administration (FDA) has granted the company’s lead clinical candidate, N91115, Orphan Drug Designation for the treatment of cystic fibrosis (CF). The ... Read more

October 16, 2015November 5, 2015

Galapagos Announces Advancement of Triple Combination Therapy into Development for Cystic Fibrosis Treatment

Cystic Fibrosis, News

Galapagos NV has announced the advancement of development plans for a triple combination Cystic fibrosis (CF) therapy consisting of GLPG2665, one of the multiple C2 correctors developed by the company, corrector ... Read more

September 28, 2015September 28, 2015

CHMP Issues Positive Recommendation for ORKAMBI and KALYDECO in the EU

News

Biotechnology company Vertex Pharmaceuticals, Inc. recently announced that the European Union Committee for Medicinal Products for Human Use (CHMP) has released a positive opinion and recommendation for Marketing Authorization of breakthrough ... Read more